Preclinical Assessment of Intrathecal rAAV9-Mediated miATM Therapy for Ataxia Telangiectasia in Mouse Models.

Principal researcher:  Professor Hilde L. Nilsen Institute: …
Sandpit Event

A-T Translational Sandpit Event

17th January 2024
Dr Caroline Blanchard

STIM A-T Pilot Study

Research Project information Principal researcher: Dr…
Virtual Reality in A-T - Prof Philip Breedon
understanding glucose metabolism defects

Understanding and correcting glucose metabolism defects in A-T

Research Project information Principal researcher: Associate…
Digital Drug Prediction - Dr Sam Nayler

Digital drug prediction informed by genetic analysis of stem cell-derived mini-brains from A-T patients

Research Project information Principal researcher: Dr…
Trial REadiness in Ataxia Telangiectasia (TREAT A-T)

Trial REadiness in Ataxia Telangiectasia (TREAT-AT)

Research Project information Principal researchers: Dr…
A-T Natural Killer Cells

Study of natural killer cells in A-T pathogenesis and their therapeutic implications

Research Project information Principal researchers: Dr…
Dr James Dixon

Brain-penetrating ATM gene therapy

Research Project information Principal researcher: Dr…
Prof Yanez-Munoz

Further development of CRISPR/Cas Genome Editing as a Treatment for Ataxia Telangiectasia

Research Project information Principal researcher: Professor…
Professor Michael Kastan

A new function for ATM and a new theory for the clinical abnormalities in A-T

Research Project information Principal researcher: Professor…
Professor Margot Mayer-Proschel

Recurrent pulmonary infections and their impact on neurological decline in A-T

Research Project information Principal researcher: Professor…
Munira Khan