Preclinical Assessment of Intrathecal rAAV9-Mediated miATM Therapy for Ataxia Telangiectasia in Mouse Models.
Principal researcher: Professor Hilde L. Nilsen
Institute: …
Modelling Ataxia Telangiectasia pathogenesis and therapeutics using human pluripotent stem cells and genetic engineering.
Principal researcher: Dr Núria Montserrat
Institute: …
A-T Translational Sandpit Event
17th January 2024
STIM A-T Pilot Study
Research Project information
Principal researcher: Dr…
Understanding and correcting glucose metabolism defects in A-T
Research Project information
Principal researcher: Associate…
Digital drug prediction informed by genetic analysis of stem cell-derived mini-brains from A-T patients
Research Project information
Principal researcher: Dr…
Trial REadiness in Ataxia Telangiectasia (TREAT-AT)
Research Project information
Principal researchers: Dr…
Study of natural killer cells in A-T pathogenesis and their therapeutic implications
Research Project information
Principal researchers: Dr…
Brain-penetrating ATM gene therapy
Research Project information
Principal researcher: Dr…
Further development of CRISPR/Cas Genome Editing as a Treatment for Ataxia Telangiectasia
Research Project information
Principal researcher: Professor…
A new function for ATM and a new theory for the clinical abnormalities in A-T
Research Project information
Principal researcher: Professor…
Recurrent pulmonary infections and their impact on neurological decline in A-T
Research Project information
Principal researcher: Professor…
The ATeam: Producing healthcare guidance for children with A-T including the exploration and design of a home-based exercise package
Research Project information
Principal researchers: Munira…
Innovative methods for gene therapy in Ataxia-Telangiectasia
Research Project information
Principal researcher: Professor…