![](https://actionforat.org/wp-content/uploads/2020/07/GStewart-profile-picture-495x400.jpg)
![](https://actionforat.org/wp-content/uploads/2024/01/Hilde-Loge-Nilsen-Oslo-University-Hospital-Norway-495x400.jpg)
Preclinical Assessment of Intrathecal rAAV9-Mediated miATM Therapy for Ataxia Telangiectasia in Mouse Models.
Principal researcher: Professor Hilde L. Nilsen
Institute: …
![](https://actionforat.org/wp-content/uploads/2024/01/Nuria-Montserrat-IBEC-Barcelona-Spain-cropped-495x400.jpg)
Modelling Ataxia Telangiectasia pathogenesis and therapeutics using human pluripotent stem cells and genetic engineering.
Principal researcher: Dr Núria Montserrat
Institute: …
![](https://actionforat.org/wp-content/uploads/2024/01/jnr-Trailblazers-Logo-2024-495x400.jpg)
2024 St Martin's School Trailblazer Walk
Trailblazers Walk - 15th June 2024
![Sandpit Event](https://actionforat.org/wp-content/uploads/2023/02/Sandpit-Event-495x400.jpg)
A-T Translational Sandpit Event
17th January 2024